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Mechanisms and Treatment of Exercise Intolerance and Persistent Fatigue in Spinal Muscular Atrophy

Columbia University · 2022
ClinicalTrials.gov · Datasets · License: Public Domain · 2022
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aerobic-capacityfatiguespinal-muscular-atrophy
spinal muscular atrophy, neuromuscular disease, risdiplam, nusinersen, aerobic capacity, oxygen uptake, fatigue, near infrared spectroscopy, muscle ultrasound, exercise tolerance, six minute walk test, mitochondria mitophagy
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Record · ID 808065
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