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An Open-Label Extension Study of GA-GCB ERT in Patients With Type 1 Gaucher Disease
gaucher disease, type 1, vpriv, enzyme replacement therapy, gaucher disease, glucocerebrosidase, beta-glucocerebrosidase, acid beta-glucocerebrosidase, glucosylceramidase, d-glucosyl-n-acylsphingosine glucohydrolase, gene activation, human, interventional
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