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Study to Assess the Safety and Efficacy of ISIS 301012 (Mipomersen) in Homozygous Familial Hypercholesterolemia
lipid metabolism, inborn errors, hypercholesterolemia, autosomal dominant, hyperlipidemias, metabolic diseases, hyperlipoproteinemia type ii, metabolism, inborn errors, genetic diseases, inborn, infant, newborn, diseases, metabolic disorder, congenital abnormalities, hypercholesterolemia, hyperlipoproteinemias
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