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GM1 and GM2 Gangliosidosis PROspective Neurological Disease TrajectOry Study (PRONTO)

Azafaros B.V. · 2022
ClinicalTrials.gov · Datasets · License: Public Domain · 2022
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genetic-diseases
gm1 gangliosidosis, sandhoff disease, tay-sachs disease, gm2 gangliosidosis, natural history study, lysosomal storage disorders, nervous system diseases, genetic diseases, inborn, hexosaminidase a and b deficiency, β-galactosidase deficiency, observational
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