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A Multi-cohort Study of Safety, Efficacy, PK and PD of GNR-055 in Patients With Mucopolysaccharidosis Type II
mucopolysaccharidosis type ii, metabolic diseases, cognitive dysfunction, lysosomal storage diseases, neurocognitive disorders, metabolism, inborn, genetic diseases, inborn, neurobehavioral manifestations, neurologic manifestations, genetic diseases, x-linked, hunter syndrome, iduronate-2-sulfatase
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