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Study of Sodium Phenylbutyrate (ACER-001) for the Treatment of Patients With Medium Chain Acyl-CoA Dehydrogenase Deficiency (MCADD)
Jerry Vockley, MD, PhD
· 2024
ClinicalTrials.gov · Datasets · License: Public Domain · 2024
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medium-chain acyl-coa dehydrogenase deficiency, medium chain acyl-coa dehydrogenase deficiency, interventional, phase2
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