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A Study of UX007 (Triheptanoin) in Participants With Long-Chain Fatty Acid Oxidation Disorders (LC-FAOD)

Ultragenyx Pharmaceutical Inc · 2014
ClinicalTrials.gov · Datasets · License: Public Domain · 2014
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long-chain fatty acid oxidation disorders (lc-faod), carnitine palmitoyltransferase (cpt ii) deficiency, very long chain acyl-coa dehydrogenase (vlcad) deficiency, longchain 3-hydroxy-acyl-coa dehydrogenase (lchad) deficiency, trifunctional protein (tfp) deficiency, faod, vlcad, cpt ii, cpt2, cpt 2, lchad, ux007
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Record · ID 852138
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