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Phase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)
muscular dystrophy, duchenne, muscular dystrophies, muscular disorders, atrophic, muscular diseases, musculoskeletal diseases, neuromuscular diseases, nervous system diseases, genetic diseases, x-linked, genetic diseases, inborn, duchenne muscular dystrophy, dystrophinopathy, nonsense mutation
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