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Phase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)

PTC Therapeutics · 2013
ClinicalTrials.gov · Datasets · License: Public Domain · 2013
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duchenne-muscular-dystrophygenetic-diseases
muscular dystrophy, duchenne, muscular dystrophies, muscular disorders, atrophic, muscular diseases, musculoskeletal diseases, neuromuscular diseases, nervous system diseases, genetic diseases, x-linked, genetic diseases, inborn, duchenne muscular dystrophy, dystrophinopathy, nonsense mutation
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Record · ID 858226
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