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Risdiplam in Patients With Spinal Muscular Atrophy Previously Treated With Nusinersen

Clinic for Special Children · 2022
ClinicalTrials.gov · Datasets · License: Public Domain · 2022
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prospectivespinal-muscular-atrophy
spinal muscular atrophy, nusinersen, prospective, risdiplam, interventional, phase4
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