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Safety and Efficacy Study of Sebelipase Alfa in Participants With Lysosomal Acid Lipase Deficiency

Alexion Pharmaceuticals, Inc. · 2014
ClinicalTrials.gov · Datasets · License: Public Domain · 2014
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lysosomal acid lipase deficiency, enzyme replacement therapy (ert), lysosomal storage disease, late onset lysosomal acid lipase (lal) deficiency, acid cholesteryl ester hydrolase deficiency, type 2, acid lipase disease, cholesterol ester hydrolase deficiency, lal deficiency, lipa deficiency, wolman disease, additional relevant mesh terms:, cholesterol ester storage disease
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Record · ID 861725
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