A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)

Name: A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)
Published: 2023
License: Public Domain

Sarepta Therapeutics, Inc. · 2023

ClinicalTrials.gov · Datasets · License: Public Domain · 2023

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duchenne-muscular-dystrophy pediatric

duchenne muscular dystrophy, dmd, gene-delivery, pediatric, north star ambulatory assessment (nsaa), performance of upper limb (pul), duchenne, interventional, phase3

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A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)

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