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Safety, Tolerability and Pharmacokinetics of SBC-102 (Sebelipase Alfa) in Adult Participants With Lysosomal Acid Lipase Deficiency
cholesterol ester storage disease(cesd), lysosomal acid lipase deficiency, lal-deficiency, enzyme replacement therapy (ert), lysosomal storage disease, late onset lysosomal acid lipase (lal) deficiency, acid cholesteryl ester hydrolase deficiency, type 2, acid lipase disease, cholesterol ester hydrolase deficiency, lal deficiency, lipa deficiency, wolman disease
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