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Study of AAVrh10-h.SGSH Gene Therapy in Patients With Mucopolysaccharidosis Type IIIA (MPS IIIA)

LYSOGENE · 2018
ClinicalTrials.gov · Datasets · License: Public Domain · 2018
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mucopolysaccharidosis type iiia, mps iiia, sanfilippo syndrome type a, lysosomal storage disease, interventional, phase2, phase3
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