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A Non-interventional, Post-Marketing Study to Describe Outcome of Nitisinone Treatment in HT-1 Patients

Swedish Orphan Biovitrum · 2025
ClinicalTrials.gov · Datasets · License: Public Domain · 2025
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chinarare-diseases
hereditary tyrosinemia, type i, rare diseases, fumarylacetoacetate hydrolase (fah) deficiency, liver failure, drug treatment, nitisinone, observational research, phase iv, china, pediatric patient, observational
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