The ENABLE Study: Safety and Efficacy Study of INZ-701 in Patients With ENPP1 Deficiency

ectonucleotide pyrophosphatase/phosphodiesterase1 deficiency, autosomal recessive hypophosphatemic rickets, generalized arterial calcification of infancy 1, hypopyrophosphatemia, enpp1, autosomal recessive hypophosphatemic rickets type 2, arhr2, generalized arterial calcification of infancy, gaci, interventional, phase2