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Volanesorsen Early Access Program for Patients With Familial Chylomicronemia Syndrome (FCS)

Akcea Therapeutics
ClinicalTrials.gov · Datasets · License: Public Domain
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lipidmetabolismmetabolicdiseases
familial chylomicronemia, familial lipoprotein lipase deficiency, hyperlipoproteinemias, familial hyperlipoproteinemia type 1, hyperlipoproteinemia type 1, hyperchylomicronemia, familial, lipoprotein lipase deficiency, familial, hyperlipidemias, dyslipidemias, lipid metabolism disorders, lipid metabolism, inborn errors, metabolic diseases
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Record · ID 966375
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