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An Open-label Study to Investigate ECUR-506 in Male Babies Less Than 9 Months of Age With Neonatal Onset OTC Deficiency

iECURE, Inc. · 2024
ClinicalTrials.gov · Datasets · License: Public Domain · 2024
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amino-acid-metabolismammoniagenetic-diseases
ornithine transcarbamylase deficiency, ornithine transcarbamylase deficiency disease, ornithine carbamoyltransferase deficiency (disorder), urea cycle disorders, inborn, amino acid metabolism, inborn errors, ammonia, brain diseases, brain diseases, metabolic, brain diseases, metabolic, inborn, central nervous system diseases, genetic diseases, inborn, genetic diseases, x-linked
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Record · ID 992088
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