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Safety and Efficacy Evaluation of GC101 Gene Therapy Via Intrathecal (IT) Injectionin the Treatment of Patients With Type 2 Spinal Muscular Atrophy (SMA) - Phase III

GeneCradle Inc · 2025
ClinicalTrials.gov · Datasets · License: Public Domain · 2025
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smaspinalmuscularatrophy
sma - spinal muscular atrophy, sma, type ii, aav gene therapy, genecradle, interventional, phase3
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