gene-therapy

Documents about gene-therapy

• Gene therapy as an upcoming technique in the treatment of cancer: A cellular solution to a cellular problem#1500320Europe PMC
• An Open Label Clinical Trial of Retinal Gene Therapy for Choroideremia#918115ClinicalTrials.gov
• A Gene Therapy Study for Hemophilia B#855739ClinicalTrials.gov
• THOR - Tübingen Choroideremia Gene Therapy Trial#846391ClinicalTrials.gov
• Gene Therapy for Pleural Malignancies#994042ClinicalTrials.gov
• Gene Therapy for Alzheimer's Disease Clinical Trial#1172681ClinicalTrials.gov
• Gene Therapy for Chinese Hemophilia A#1093158ClinicalTrials.gov
• Safety and Efficacy of Injectable Klotho Plasmid Gene Therapy in Humans#837272ClinicalTrials.gov
• Gene Therapy for Pyruvate Kinase Deficiency (PKD)#1420067ClinicalTrials.gov
• Addressing the Limits of Emx2 Therapy of Glioblastoma Multiforme by Transgene Insulation and Epigenetic Pharmacological Intervention#1133215Europe PMC
• Gene Therapy for Chronic Granulomatous Disease in Korea#805282ClinicalTrials.gov
• Gene Therapy for WAS#805485ClinicalTrials.gov
• Safety and Efficacy of Klotho and Follistatin Gene Therapy#913988ClinicalTrials.gov
• Gene Therapy for Gyrate Atrophy#1114726ClinicalTrials.gov
• Evaluation of Safety and Tolerability of Libella Gene Therapy for Critical Limb Ischemia: AAV- hTERT#1164061ClinicalTrials.gov
• Gene Therapy Trial for Platelet Derived Factor VIII Production in Hemophilia A#905854ClinicalTrials.gov
• Gene Therapy for ADA-SCID#1337454ClinicalTrials.gov
• Bridging science and hope: the evolving story of gene therapy for neuromuscular diseases#157662HAL (France)
• Liver Biopsy Following Gene Therapy For Hemophilia#899122ClinicalTrials.gov
• Clinical Characterization on PDE6A-related Retinitis Pigmentosa in Preparation to a Gene Therapy Trial#1485743ClinicalTrials.gov
• Non-Viral TCR Gene Therapy#1058081ClinicalTrials.gov
• Safety and Efficacy of GS-100 Gene Therapy in Patients With NGLY1 Deficiency#1195392ClinicalTrials.gov
• Gene Therapy for Wiskott-Aldrich Syndrome (WAS)#1057420ClinicalTrials.gov
• rAd-p53 Gene Therapy for Advanced Oral and Maxillofacial Malignant Tumors#859360ClinicalTrials.gov
• Therapeutic frontiers in ALS: iPSC-based drug discovery, cell therapy, and gene therapy-Advances through 2026#353872Europe PMC
• A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH)#812694ClinicalTrials.gov
• A Study of AB-1005 Gene Therapy in Japanese Adults With Moderate Parkinson's Disease (J-REGENERATE-PD)#1125085ClinicalTrials.gov
• A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)#1385165ClinicalTrials.gov
• A Gene Therapy Study of BMN 331 in Subjects With Hereditary Angioedema#858741ClinicalTrials.gov
• Needs Assessment of Knowledge, Beliefs, and Attitudes of Patients With Hemophilia B About Gene Therapy#882323ClinicalTrials.gov
• 4D-150 in Patients With Diabetic Macular Edema#1128210ClinicalTrials.gov
• Safety and Efficacy Study of Gene Therapy for Acute Myocardial Infarction in Korea#1283067ClinicalTrials.gov
• Safety and Efficacy Study of Novel Gene Therapy ZM-02 for Retinitis Pigmentosa Patients#1466141ClinicalTrials.gov
• Phase I Gene Therapy Clinical Trial Using the Vector rAAV2/5-PBGD for the Treatment of Acute Intermittent Porphyria#915564ClinicalTrials.gov
• The Endovascular Plus GENe Therapy Versus Only EndoVascular Therapy for Severe Limb ischaemiA Trial#1047834ClinicalTrials.gov
• A Study to Understand the Long-term Safety and Effects of an Experimental Gene Therapy for Duchenne Muscular Dystrophy.#1244143ClinicalTrials.gov
• Gene Therapy for ACM Due to a PKP2 Pathogenic Variant#1095332ClinicalTrials.gov
• Quantification of Ocular Gene Therapy-Related Inflammation Using the VRMACS Grading System#676440Europe PMC
• A Phase I Gene Therapy Study of FP253/Fludarabine for Prostate Cancer#801591ClinicalTrials.gov
• A Safety Study of Retinal Gene Therapy for Choroideremia With Administration of BIIB111#825416ClinicalTrials.gov
• A Phase 3 Study Of OCU400 Gene Therapy for the Treatment Of Retinitis Pigmentosa#841993ClinicalTrials.gov
• Safety Study of RPE65 Gene Therapy to Treat Leber Congenital Amaurosis#849647ClinicalTrials.gov
• Randomized Trial of Suicide Gene Therapy and Prostate Cancer#905560ClinicalTrials.gov
• An Exploration of the Impact of Gene Therapy on the Lives of People With Haemophilia and Their Families#1338377ClinicalTrials.gov
• Methodology Study of Retroviral Insertion Site Analysis in Strimvelis Gene Therapy#1378547ClinicalTrials.gov
• Safety Study of Subthalamic Nucleus Gene Therapy for Parkinson's Disease#1484666ClinicalTrials.gov
• Studies of the adenovirus 5 L1 gene aimed at developing L1 gene deficiencies for use in gene therapy vectors#1298727Europe PMC
• Gene Therapy Study for Children With CLN5 Batten Disease#803687ClinicalTrials.gov
• Gene Therapy for the Treatment of Brain Tumors#1184851ClinicalTrials.gov
• Antisense-Oligonucleotide Gene Therapy for KCNC1-Related Developmental and Epileptic Encephalopathy#297899ScholarlyCommons at Penn