gene-therapy

Documents about gene-therapy

• Vector Delivery of the IL-12 Gene in Men With Prostate Cancer#992737ClinicalTrials.gov
• Current Status of Clinical Trials Design and Outcomes in Retinal Gene Therapy#360971PubMed Central
• Gene replacement therapy for centronuclear myopathy: A breakthrough in complex genetic muscle disease#434532OKAYAMA UNIVERSITY SCIENTIFIC ACHIEVEMENT REPOSITORY
• Patient Self-management and Gene Guided Therapy for Chronic Hepatitis C#863398ClinicalTrials.gov
• Quaratusugene Ozeplasmid (Reqorsa) and Atezolizumab Maintenance Therapy in ES-SCLC Patients#862357ClinicalTrials.gov
• Gene Therapy for Chronic Granulomatous Disease#908159ClinicalTrials.gov
• Long Term Follow Up Of Patients Who Have Received Gene Therapy Or Gene Marked Products#683131ClinicalTrials.gov
• Relationship Between Body Composition, Food Consumption, and Micro and Macronutrients With Gene Expression in Breast Cancer#868069ClinicalTrials.gov
• Synergistic antioxidant and gene supplementation for high-efficacy retinitis pigmentosa therapy.#182536NCBI PubMed Central
• Toward Safe and Effective Gene Therapy: Non-Viral Nanostructured Delivery Systems.#385218NCBI PubMed Central
• Impact of Prolonged Antibiotic Therapy on Commensal Microbial Community Gene Expression.#451489ClinicalTrials.gov
• Ecological Models for Gene Therapy. II. Niche Construction, Nongenetic Inheritance, and Ecosystem Perturbations#761144PhilArchive
• AAV Gene Therapy Study for Subjects with PKU#853578ClinicalTrials.gov
• Long Term Follow-Up for RGX-111#856012ClinicalTrials.gov
• Long-term Follow-up of Sanfilippo Type A Patients Treated by Intracerebral SAF-301 Gene Therapy#828609ClinicalTrials.gov
• Principles and practices for successful gene therapy innovative contracting: Insights from a multistakeholder convening.#335939PubMed
• The Effects of Short-term Preoperative Treatment With Hormonal Therapy on Gene Profiles in Breast Cancer#894473ClinicalTrials.gov
• Reprogramming innate immunity through viral interference: A double-edged strategy for enhancing and containing gene therapies#123215Europe PMC
• DEVELOPING GENOME EDITING THERAPIES FOR RARE AND ULTRA-RARE METABOLIC DISEASES#929129ScholarlyCommons
• South America and Mexico's cell and gene therapy landscape: accelerating growth and persistent challenges.#419063PubMed
• Nano-Embedded Bioplatform for Ocular Delivery of Genetic Material#673206WIReDSpace
• The Symphony Triple A Study: Using Symphony in Treatment Decisions Concerning Adjuvant Systemic Therapy#871198ClinicalTrials.gov
• Phase II High Risk Prostate Cancer Trial Using Gene & Androgen Deprivation Therapies, Radiotherapy, & Surgery#875765ClinicalTrials.gov
• Artificial Intelligence and the Transformation of Cell and Gene Therapy Development.#848NCBI PubMed Central
• Extension of Phase 3 Gene Therapy for Painful Diabetic Neuropathy#184780ClinicalTrials.gov
• Antioxidant lipid nanoparticles enhance mRNA stability for regeneration therapy and gene editing#408718HAL (France)
• A Gene Therapy Study in Patients With Gaucher Disease Type 1#860815ClinicalTrials.gov
• A Phase 1 AAV Gene Therapy Trial Evaluating Safety and Preliminary Efficacy of RP-A701 in Subjects With BAG3 Dilated Cardiomyopathy#908330ClinicalTrials.gov
• Base-Edited Hematopoietic Stem/Progenitor Cell Gene Therapy for Treatment of CXCR4-WHIM#852492ClinicalTrials.gov
• Epitranscriptomic Remodeling of N6-Methyladenosine (m6A) RNA Marks in CRISPR-Edited Genomes: Emerging Implications for Off-Target Genetic Instability and Precision Gene Therapy#303039Zenodo (CERN)
• Suicide Gene Therapy for Donor Lymphocytes Infusion After Allogeneic Hematopoietic Stem Cell Transplantation#123460ClinicalTrials.gov
• Optimization of AAV tools to target M&uumlller glial cells for retinal gene therapy#170846bioRxiv / medRxiv
• Comparative Clinical Outcomes of Nusinersen and Gene Therapy in Spinal Muscular Atrophy Type 1#325999HAL (France)
• Gene Therapy for Amino Acid Decarboxylase Deficiency: Clinical and Imaging Outcomes in a French Cohort#337495HAL (France)
• Safety and Efficacy of p53 Gene Therapy Combined With Immune Checkpoint Inhibitors in Solid Tumors.#343815ClinicalTrials.gov
• Three-Month Observational Data for the MPS IIIB Sentinel Subject Following AAV9 Mediated Gene Therapy#349766bioRxiv / medRxiv
• FMR1 gene therapy restores activity-driven inhibition and prevents audiogenic seizures in Fmr1-/y mice#369701bioRxiv / medRxiv
• Combining gene and stem cell therapy in the treatment of dysferlinophaties#392064IRIS
• Immunotherapy Treating GI Cancer#840663ClinicalTrials.gov
• Long-Term Follow-Up Gene Therapy Study for Achromatopsia CNGB3 and CNGA3#886557ClinicalTrials.gov
• Intracerebral Gene Therapy in Children With Sanfilippo Type B Syndrome#895979ClinicalTrials.gov
• AAV9 U7snRNA Gene Therapy to Treat Boys With DMD Exon 2 Duplications.#901257ClinicalTrials.gov
• ATSN-201 Gene Therapy in RS1-Associated X-linked Retinoschisis#1030033ClinicalTrials.gov
• Discovering a Novel AAV2-Based Capsid for RPE Transduction via Intravitreal Injection in rd12 Mice for Leber Congenital Amaurosis Type 2 Gene Therapy#634876eScholarship
• Safety and Tolerability of Intravitreal Administration of VG901 in Patients With Retinitis Pigmentosa Due to Mutations in the CNGA1 Gene#847603ClinicalTrials.gov
• Gene Transfer Study of ABO-102 in Patients With Middle and Advanced Phases of MPS IIIA Disease#1007520ClinicalTrials.gov
• Gene Therapy Trial for Otoferlin Gene-mediated Hearing Loss#831960ClinicalTrials.gov
• Base Editing Hematopoietic Stem Cell and T Cell Gene Therapy for CD40L-HyperIgM Syndrome: Single Patient Study#878235ClinicalTrials.gov
• Towards a Comprehensive Screening Approach for Detecting Gene Doping in Racehorses and Sport Horses by Targeting Common and Intrinsic Plasmid Sequences#1039029HAL (France)
• Targeting Neurovascular Pathways: Gene Therapy as a Novel Treatment for Vascular Dementia After Stroke.#150144NCBI PubMed Central