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Documents about rett-syndrome
- ASSESSING EMERALD AND MC10 BIOSTAMP nPOINT BIOSENSORS FOR RETT SYNDROME#1007902ClinicalTrials.gov
- A Safety Study of NNZ-2566 in Pediatric Rett Syndrome#831478ClinicalTrials.gov
- A Safety Study of NNZ-2566 in Patients With Rett Syndrome#894547ClinicalTrials.gov
- Effects of Creatine Supplementation in Rett Syndrome#1431434ClinicalTrials.gov
- Metabolic Evaluation of Nutrition in Rett Syndrome#1438859ClinicalTrials.gov
- Neurophysiologic Biomarkers in Rett Syndrome#870086ClinicalTrials.gov
- A Phase 1/2/3 Study of TSHA-102 Gene Therapy in Females With Rett Syndrome (REVEAL Pivotal Study)#1398224ClinicalTrials.gov
- A Study to Evaluate Ketamine for the Treatment of Rett Syndrome#878775ClinicalTrials.gov
- Functional Abilities in Rett Syndrome#898197ClinicalTrials.gov
- Patients With RETT Syndrome#1033350ClinicalTrials.gov
- Rett Syndrome Registry#894600ClinicalTrials.gov
- Validating Innovative Biosensors for Rett Autonomic Symptom Tracking#1294467ClinicalTrials.gov
- Open Label Trial of Triheptanoin (UX007) in Treatment of Rett Syndrome.#1212617ClinicalTrials.gov
- Analysis of the Glutathione Cycle in Children With Rett Syndrome#855757ClinicalTrials.gov
- GCB-002 in Treatment of Patients With Rett Syndrome#864582ClinicalTrials.gov
- A Phase 3 Study of Fenfluramine Hydrochloride in Rett Syndrome#195451ClinicalTrials.gov
- The Diagnostic Experience of Male Rett Syndrome#1033136ClinicalTrials.gov
- ANAVEX2-73 Study in Patients With Rett Syndrome#866909ClinicalTrials.gov
- Osteopathic Manipulative Treatment for Constipation in People With Rett Syndrome#967606ClinicalTrials.gov
- Creatine Metabolism in Rett Syndrome#1350640ClinicalTrials.gov
- 'Uptime' Participation Intervention in Girls and Women With Rett Syndrome#1171555ClinicalTrials.gov
- An Exploratory Trial of Ketamine for the Treatment of Rett Syndrome#1336887ClinicalTrials.gov
- ANAVEX2-73 Study in Pediatric Patients With Rett Syndrome#1483672ClinicalTrials.gov
- To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome#1350988ClinicalTrials.gov
- Natural History of Rett Syndrome & Related Disorders#992832ClinicalTrials.gov
- Rett REVOLUTION Trial: An Exploratory Evaluation of the Safety and Efficacy of Vorinostat in Rett Syndrome#1439431ClinicalTrials.gov
- Biobanking of Rett Syndrome and Related Disorders#851205ClinicalTrials.gov
- Study of Trofinetide for the Treatment of Girls and Women With Rett Syndrome (LAVENDER™)#913408ClinicalTrials.gov
- Lamivudine as a Novel Clinical Effort for Rett Syndrome#1171508ClinicalTrials.gov
- Leptin antagonism improves Rett syndrome phenotype in symptomatic Mecp2-deficient mice#231638HAL (France)
- Treatment of Rett Syndrome With Recombinant Human IGF-1#1072391ClinicalTrials.gov
- Technology-supported Motor Rehabilitation for People With Rett Syndrome#1307467ClinicalTrials.gov
- Tolerability of the Immersive Virtual Reality System Grail in Subjects Affected by Rett Syndrome#1182461ClinicalTrials.gov
- Telehealth Support to Increase Physical Activity in Rett Syndrome#1352380ClinicalTrials.gov
- The Role of Family Functioning in Adaptation to Being a Caregiver of an Individual With Rett Syndrome#1292503ClinicalTrials.gov
- The Role of Dietary Calcium for the Treatment of Osteopenia in Girls With Rett Syndrome#1465161ClinicalTrials.gov
- Increased Osteoclast Activity Contributes to Bone Resorption and Osteopenia in a Rett Syndrome Mouse Model#239008HAL (France)
- Nutritional Aspects of Rett Syndrome#1059377ClinicalTrials.gov
- Efficacy and Safety of Cannabidiol Oral Solution (GWP42003-P, CBD-OS) in Patients With Rett Syndrome#1475352ClinicalTrials.gov
- Rare Diseases Clinical Research Network: Neurophysiological Correlates#838180ClinicalTrials.gov
- An Open-Label Study of Trofinetide for the Treatment of Girls Two to Five Years of Age Who Have Rett Syndrome#907693ClinicalTrials.gov
- Alteration of cholinergic pathway in the enteric nervous system of a mouse model of Rett syndrome#677064HAL (France)
- A Long-term Safety Study of Cannabidiol Oral Solution (GWP42003-P, CBD-OS) in Patients With Rett Syndrome#902384ClinicalTrials.gov
- Single-Dose AAV-MECP2 Safety/Tolerability and Efficacy in Rett Syndrome#1308620ClinicalTrials.gov
- To Study the Efficacy & Safety of Oral NA-921 (Bionetide) in Girls and Women with Rett Syndrome#1462724ClinicalTrials.gov
- Independent Studies of Dextromethorphan and of Donepezil Hydrochloride for Rett Syndrome#993699ClinicalTrials.gov
- Sleep Abnormalities in Rare Genetic Disorders: AS, RTT, and PW#810062ClinicalTrials.gov
- Angelman & Rett Syndrome: Interaction and Communication#1307828ClinicalTrials.gov
- Distribution of hand function by age in individuals with Rett syndrome#431471PubMed Central
- Impaired astrocyte-to-neuron cholesterol trafficking drives synaptic dysfunction in Rett syndrome#610848bioRxiv / medRxiv
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