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A Study Of PGN-EDO51 In Participants With Duchenne Muscular Dystrophy Amenable To Exon 51-Skipping Treatment
duchenne muscular dystrophy, enhanced delivery oligonucleotide, peptide-conjugated phosphorodiamidate, morpholino oligomer, oligonucleotide, exon 51, next-generation oligonucleotide, cell-penetrating peptide, muscular dystrophies, neuromuscular disease, dystrophin production, splice correcting oligonucleotide
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