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Efficacy Confirmation Study of NPC-09

Nobelpharma · 2021
ClinicalTrials.gov · Datasets · License: Public Domain · 2021
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gne myopathy, distal myopathy with rimmed vacuoles (dmrv), hereditary inclusion body myopathy (hibm), nonaka disease, sialic acid, aceneuramic acid, n-acetylneuraminic acid, interventional, phase3
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