Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-318 in Subjects With MPS I

Name: Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-318 in Subjects With MPS I
Published: 2017
License: Public Domain

Sangamo Therapeutics · 2017

ClinicalTrials.gov · Datasets · License: Public Domain · 2017

Open Source ↗

dna gene-editing gene-therapy genetic

mps i, mucopolysaccharidosis i, hurler-scheie syndrome, gene therapy, gene editing, zinc finger, sb-318, rare, genetic, dna, sangamo, genome editing

This document is indexed with metadata only — full text is not available in the archive for this record. Open the official source ↗

Record · ID 867567
Retrieved via Conceptio — every document is proof-bundled with source, license, and retrieval metadata.