Single-Arm Study To Evaluate The Efficacy and Safety of Valoctocogene Roxaparvovec in Hemophilia A Patients at a Dose of 4E13 vg/kg

Name: Single-Arm Study To Evaluate The Efficacy and Safety of Valoctocogene Roxaparvovec in Hemophilia A Patients at a Dose of 4E13 vg/kg
Published: 2018
License: Public Domain

BioMarin Pharmaceutical · 2018

ClinicalTrials.gov · Datasets · License: Public Domain · 2018

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genetherapy geneticdiseases

hemophilia a, gene therapy, clotting disorders, blood disorder, blood coagulation disorders, inherited blood coagulation disorders, hematologic diseases, coagulation protein disorders, hemorrhagic disorders, genetic diseases, inborn, factor viii

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Record · ID 913184
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