ClinicalTrials.govpublic full text
RGX-111 Gene Therapy in Patients With MPS I
mucopolysaccharidosis type i (mps i), hurler syndrome, hurler-scheie syndrome, mps i , gene therapy, hurler, hurler- scheie, interventional, phase1, phase2
This document is indexed with metadata only — full text is not available in the archive for this record.
Open the official source ↗
Related documents
Record · ID 966766
Retrieved via
Conceptio — every document is proof-bundled with source, license, and retrieval metadata.