Safety, Tolerability, and Exploratory Efficacy Study of Intrathecally Administered Gene Therapy AMT-162 in Adult Participants With SOD1 Amyotrophic Lateral Sclerosis (SOD1-ALS)

Name: Safety, Tolerability, and Exploratory Efficacy Study of Intrathecally Administered Gene Therapy AMT-162 in Adult Participants With SOD1 Amyotrophic Lateral Sclerosis (SOD1-ALS)
Published: 2024
License: Public Domain

UniQure Biopharma B.V. · 2024

ClinicalTrials.gov · Datasets · License: Public Domain · 2024

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als amyotrophiclateralsclerosis genetherapy

amyotrophic lateral sclerosis, gene therapy, aav (adeno-associated virus), als, sod1, interventional, phase1, phase2

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Safety, Tolerability, and Exploratory Efficacy Study of Intrathecally Administered Gene Therapy AMT-162 in Adult Participants With SOD1 Amyotrophic Lateral Sclerosis (SOD1-ALS)

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