adeno

Documents about adeno

• Human and Insect Cell-Produced Recombinant Adeno-Associated Viruses Show Differences in Genome Heterogeneity#176852HAL (France)
• Safety and Dose-escalation Study of AAV2-hCHM in Participants With CHM (Choroideremia) Gene Mutations#804093ClinicalTrials.gov
• Fatal thrombotic microangiopathy case following adeno-associated viral SMN gene therapy#254049HAL (France)
• Test rapid ROTA/ADENO/NORO /ASTRO#208636EU Publications
• Preemptive Dexamethasone , Paracetamol on Postoperative Period Following Adeno-tonsillectomy in Pediatric .#850569ClinicalTrials.gov
• microRNA Profiles Identification in Adeno Carcinoma Prostate Cancer#966903ClinicalTrials.gov
• Durable protection against SIV challenge by adeno-associated virus delivery of Env-specific antibodies#216629bioRxiv / medRxiv
• A Prospective Study Evaluating Seroprevalence and Seroconversion of Antibodies Against Adeno-associated Virus (AAV)#994886ClinicalTrials.gov
• Hydrogen Peroxide Imaging via HyPer7 Probe in Adeno Associated Virus-Transduced Primary Mouse Hepatocytes.#457666NCBI PubMed Central
• KMT2D loss drives adeno-to-squamous transition and sensitizes TKI-resistant lung cancer to AURKA inhibition.#354686NCBI PubMed Central
• Small RNA Barcodes for Sensitive Labeling of AAV Transcripts#651809Europe PMC
• Mechanisms of Adeno-Associated Virus Serotype 9 Vector Characterization and Quality Control through Solid-State Nanopores.#170628NCBI PubMed Central
• Applications of adeno-associated virus for 3D single-cell morphometric analysis in iPSC-derived midbrain organoids.#271974bioRxiv / medRxiv
• Adeno-Associated Virus Gene Therapy for Spinal Muscular Atrophy Induces Hepatotoxicity via Cytokine and Macrophage Activation.#342608NCBI PubMed Central
• Recombinant adeno-associated virus-mediated HSV-TK/GCV gene therapy for ovarian cancer: an experimental study.#368183NCBI PubMed Central
• Gene Therapy Clinical Study in Adult PKU#994392ClinicalTrials.gov
• Classification and quantification of full vs. empty adeno-associated virus reference capsids via infrared attenuated total reflection spectroscopy.#222952NCBI PubMed Central
• Adeno-tonsillectomy in Treatment of Obstructive Sleep Apnea#866307ClinicalTrials.gov
• Adeno-Associated virus-based approaches for mitochondrial diseases: advances and challenges#431849Springer Nature OA
• A Study of FVIII Gene Therapy for Hemophilia A#813855ClinicalTrials.gov
• Aquaporin-1 gene therapy as a novel method to treat radiation-induced salivary gland damage: The case for adeno-associated virus vectors.#458712NCBI PubMed Central
• A Phase 1/2 Study of SHP648, an Adeno-Associated Viral Vector for Gene Transfer in Hemophilia B Subjects#848301ClinicalTrials.gov
• A Long Term Follow-up Study of Subjects Who Received ICM-203 or Matching Placebo#993099ClinicalTrials.gov
• Optimizing Cortical Neuron Labeling in vitro for Characterizing Cell Morphology#297895ScholarlyCommons at Penn
• LTFU for Gene Transfer Subjects With Hemophilia B#908832ClinicalTrials.gov
• Safety and Efficacy of Recombinant Adeno-Associated Virus Containing the CFTR Gene in the Treatment of Cystic Fibrosis#912547ClinicalTrials.gov
• Multivariate analysis of Pleurodeles waltl injection outcomes using FAMD FactoMineR (RStudio 4.3.2) used to probe sources of variability during an Adeno-associated viral (AAV) screen#653004ISTA Publications
• Progress and challenges in intrathecal gene therapy for neurological disorders#227266Europe PMC
• Enhanced recombinant adeno-associated virus (rAAV) biomanufacturing: Design of experiment (DOE) enabled transfection optimization for maximum full capsid yield and robust scale-up#359175ULRR
• A Study Evaluating the Safety, Tolerability, and Activity of ICM-203 in Subjects With Knee Osteoarthritis.#873077ClinicalTrials.gov
• Safety and Efficacy of rAAV-hRS1 in Patients With X-linked Retinoschisis (XLRS)#992570ClinicalTrials.gov
• Bio-inspired polyphenol-polyelectrolyte WRAP system for geometrically controlled AAV delivery in diverse anatomical sites#425862S-Space: Seoul National University
• Host determinants of exo-rAAV production revealed by extended gene expression analysis in HEK293 cells.#928216Repisalud
• The interaction between virus-bound KLF4 and host-bound PARP1 directs the localization of wild-type adeno-associated virus type 2 (wtAAV2) to cellular sites of DNA damage.#209523NCBI PubMed Central
• Safety Study of an Adeno-associated Virus Vector for Gene Therapy of Leber's Hereditary Optic Neuropathy#966498ClinicalTrials.gov
• A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)#891947ClinicalTrials.gov
• A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of Single Intravenous Infusion of JWK007 in Patients With Duchenne Muscular Dystrophy (DMD)#898193ClinicalTrials.gov
• Safety and Pharmacodynamics of GNSC-001 Intra-articular Injection for Knee Osteoarthritis#801380ClinicalTrials.gov
• Safety and Tolerability Subretinal OPGx-001 for LCA5-Associated Inherited Retinal Degeneration (LCA5-IRD) and Non-interventional Arm With Untreated Patients#873942ClinicalTrials.gov
• Variability in the circulation of cerebrospinal fluid: causes and clinical implications for intraventricular drug delivery#235107HAL (France)
• Safety and Efficacy Study in Subjects With Leber Congenital Amaurosis#862437ClinicalTrials.gov
• A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1#847146ClinicalTrials.gov
• Safety, Tolerability, and Exploratory Efficacy Study of Intrathecally Administered Gene Therapy AMT-162 in Adult Participants With SOD1 Amyotrophic Lateral Sclerosis (SOD1-ALS)#995492ClinicalTrials.gov
• A Phase 2 Open-label Study to Evaluate the Safety of Laruparetigene Zovaparvovec Administered Bilaterally in Male Participants With X-Linked Retinitis Pigmentosa#842772ClinicalTrials.gov
• Safety and Efficacy in LPL-Deficient Subjects of AMT-011, an Adeno-Associated Viral Vector Expressing Human Lipoprotein Lipase [S447X]#844638ClinicalTrials.gov
• Long-term Follow-up of Sanfilippo Type A Patients Treated by Intracerebral SAF-301 Gene Therapy#828609ClinicalTrials.gov
• CALM-AF-AI: Counteracting Age-related Loss of Muscle With AAV-Follistatin Combined With Angiogenesis-Inducing VEGF Plasmid Gene Therapy#807185ClinicalTrials.gov
• Supplementary Dataset 2. Process and cost-related dataset for comparative analysis of recombinant adeno-associated virus upstream manufacturing platforms#348039KU Leuven RDR Dataverse OAI Archive
• Durability of efficacy, safety, and quality of life 5 years after valoctocogene roxaparvovec gene transfer for severe hemophilia A: final phase 3 GENEr8-1 trial results#475955HAL (France)
• A Gene Transfer Study for Hemophilia A#826644ClinicalTrials.gov