gene-editing

Knowledge-graph topic · documents ABOUT gene-editing across the archive

31Documents about gene-editing

Documents about gene-editing

Generation and characterization of a human iPSC cell line expressing inducible Cas9 in the "safe harbor" AAVS1 locus#646713Repisalud
A Study to Evaluate the Safety and Pharmacokinetics of RC001 in Children With Dravet Syndrome#845758ClinicalTrials.gov
Enhancing endonuclease based gene editing in primary cells — Seattle Children's Hospital (dba Seattle Children's Research Institute) (US20200377911A1)#607215Google Patents
Improved genome editing by an engineered CRISPR-Cas12a#983366eScholarship
Method for improving plant genetic transformation and gene editing efficiency — Institute Of Genetics And Developmental Biology, Chinese Academy Of Sciences (US12416013B2)#607211Google Patents
PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)#966167ClinicalTrials.gov
Figure 1 from: Abuhaliema A, Gharaibeh L, Jaradat E, Hammad M, Alshaer W (2026) Non-coding RNAs in gene therapy: mechanisms, delivery strategies, and clinical translation. Pharmacia 73: 1-25. https://doi.org/10.3897/pharmacia.73.e173259#210307Zenodo (CERN)
The Development of a CRISPR-Based Calibrated Functional Assay for Classifying Pathogenicity of MSH2 and MSH6 Variants in Lynch Syndrome#291100Digital Commons @ UConn

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