duchenne-muscular-dystrophy

Documents about duchenne-muscular-dystrophy

• Vasodilator and Exercise Study for DMD (VASO-REx)#800520ClinicalTrials.gov
• Gentamicin Treatment of Muscular Dystrophy#867820ClinicalTrials.gov
• An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophy#832196ClinicalTrials.gov
• The Preventive Efficacy of Carvedilol on Cardiac Dysfunction in Duchenne Muscular Dystrophy#877878ClinicalTrials.gov
• A Study to Evaluate the Safety and Tolerability of Rituxan in Duchenne Muscular Dystrophy#884274ClinicalTrials.gov
• Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy#885034ClinicalTrials.gov
• Analysis of a Virtual Reality Task in Patients With Duchenne Muscular Dystrophy#981998ClinicalTrials.gov
• Halt cardiomyOPathy progrEssion in Duchenne (HOPE-OLE)#882803ClinicalTrials.gov
• Study Safety and Efficacy of Bone Marrow Derived Autologous Cells for the Treatment of Muscular Dystrophy.#911761ClinicalTrials.gov
• Biomechanical Analysis of Gait in Individuals With Duchenne Muscular Dystrophy#910616ClinicalTrials.gov
• Phase III Randomized, Double-Blind Study of Prednisone for Duchenne Muscular Dystrophy#868227ClinicalTrials.gov
• A Randomized, Double-blind, Placebo-controlled Study of Delandistrogene Moxeparvovec (SRP-9001) for Duchenne Muscular Dystrophy (DMD)#869619ClinicalTrials.gov
• Usability and User Experience of a Virtual Reality Rehabilitation Game Platform in Individuals With Duchenne Muscular Dystrophy#992705ClinicalTrials.gov
• NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)#857028ClinicalTrials.gov
• PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)#966167ClinicalTrials.gov
• Open Label Study of GSK2402968 in Subjects With Duchenne Muscular Dystrophy#909681ClinicalTrials.gov
• Neurobehavioral Profiles in Young Steroid-Naive Boys With Duchenne Muscular Dystrophy: A Baseline Data Analysis From the FOR-DMD Trial#312170IRIS
• FDA-approved antisense oligonucleotide therapies for duchenne muscular dystrophy: current status and future outlook#314819Europe PMC
• Replication Data for: Vandekerckhove et al.(2024) - Gait classification for growing children with Duchenne muscular dystrophy#418122KU Leuven RDR Dataverse OAI Archive
• Does randomization matter in rare disease clinical trials#637004PLOS
• Kinesiology Taping in Duchenne Muscular Dystrophy: Effects on Performance, Gait Characteristics, and Energy Consumption#991795ClinicalTrials.gov
• Endomysial Fibrosis, Muscular Inflammatory Response and Calcium Homeostasis Dysfunction in Duchenne Muscular Dystrophy#872955ClinicalTrials.gov
• Long-term, Extension Study of DS-5141b in Patients With Duchenne Muscular Dystrophy#846905ClinicalTrials.gov
• This is a Study to Get More Information About Non Ambulatory Boys & Men With Duchenne Muscular Dystrophy#894868ClinicalTrials.gov
• Safety and Efficacy of KER-065 in Participants With Duchenne Muscular Dystrophy#910304ClinicalTrials.gov
• Assessing movement quality in individuals with Duchenne muscular dystrophy utilizing accelerometry: Comparisons with healthy controls#251486PLOS
• Spironolactone Versus Prednisolone in DMD#967219ClinicalTrials.gov
• Nebivolol for the Prevention of Left Ventricular Systolic Dysfunction in Patients With Duchenne Muscular Dystrophy#967440ClinicalTrials.gov
• A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD)#835413ClinicalTrials.gov
• Hyperactivity, compulsive-like behaviours, and impaired flexibility in mouse models of Duchenne muscular dystrophy#11579HAL (France)
• A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)#913369ClinicalTrials.gov
• Study Determining the Frequency of Duchenne Muscular Dystrophy and Late-onset Pompe Disease#991847ClinicalTrials.gov
• How Can Different Forms of Strengthening Exercises Affect the Muscular Tissue and Its Chemical Markers in Children With Duchenne Muscular Dystrophy#883325ClinicalTrials.gov
• The Validation Process for Confirmation of the French Version of the Pediatric Quality of Life Inventory :PedsQLTM.#912254ClinicalTrials.gov
• Long-Term Extension Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon Skipping to Evaluate the Safety and Efficacy of Endosomal Escape Vehicle Phosphorodiamidate Morpholino Oligomer Platform Products (ELEVATE-LTE)#1032388ClinicalTrials.gov
• Current Standards and Future Directions of Duchenne Muscular Dystrophy Respiratory Care: The PPMD Italy Meeting Report#274656IRIS
• Dystrophin-gene mutation location influences severity of electroretinogram defects in mouse models of Duchenne muscular dystrophy#398744HAL (France)
• Effect of Oral Glutamine on Muscle Mass and Function in Duchenne Muscular Dystrophy#864777ClinicalTrials.gov
• A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of Single Intravenous Infusion of JWK007 in Patients With Duchenne Muscular Dystrophy (DMD)#898193ClinicalTrials.gov
• Effectiveness of pharmacological treatments in Duchenne muscular dystrophy: A protocol for a systematic review and meta-analysis#947705Repositorio de Universidad Autónoma de Chile.
• Optical coherence tomography findings in Duchenne muscular dystrophy.#150173NCBI PubMed Central
• Givinostat for treating Duchenne muscular dystrophy in people 6 years and over#348232NCBI Bookshelf
• Axonopathy in Duchenne Muscular Dystrophy limits microdystrophin gene therapy efficacy#779347bioRxiv / medRxiv
• Development of capillary electrophoresis method to measure albumin thiol oxidation in dystrophic humans and animal models of Duchenne muscular dystrophy#156040HAL (France)
• ANXA11 suppression restores muscular function in the mdx mouse model of Duchenne muscular dystrophy (DMD).#371498NCBI PubMed Central
• Molecular Analysis of Patients With Neuromuscular Disease#842533ClinicalTrials.gov
• Accuracy of the molecular diagnosis of duchenne and becker muscular dystrophy: A systematic review with meta-analysis#389535PLOS
• Safety, Tolerability and Effects of L-Arginine in Boys With Dystrophinopathy on Corticosteroids#876013ClinicalTrials.gov
• A Study Of PGN-EDO51 In Participants With Duchenne Muscular Dystrophy Amenable To Exon 51-Skipping Treatment#1007452ClinicalTrials.gov
• PDE Inhibitors in DMD Study (Acute Dosing Study)#880271ClinicalTrials.gov